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#基因疗法#

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基因疗法

2020-05-29

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2025-03-20发表于江苏省

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#基因疗法# #Danon病#

《新英格兰杂志》：AAV9.LAMP2B基因疗法在Danon病中的应用

2025-03-13发表于陕西省

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2025-02-27发表于上海

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2025-01-06发表于上海

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#基因疗法# #Danon病# #RP-A501#

单次输注，多个心功能指标均改善！NEJM：基因疗法有望打破这种病“无药可治”局面

2024-11-21发表于陕西省

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#基因疗法# #B型血友病#

《新英格兰杂志》：Fidanacogene Elaparvovec 基因疗法治疗B型血友病的临床研究

2024-10-16发表于上海

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#基因疗法# #CALD# #脑性肾上腺脑白质营养不良#

NEJM：从80%患儿无药可治，到94%患儿病情稳定，基因疗法逆转致命疾病困局

2024-10-15发表于上海

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#糖尿病# #基因疗法#

《自然》子刊：基因疗法“治愈”糖尿病的4大策略和广阔前景

2024-10-08发表于上海

梅斯管理员

#基因疗法# #基因递送# #细胞外液粘度#

毛海泉教授，最新Nature Chemical Engineering：调节细胞外液粘度可提高转染效率

2024-09-18发表于上海

梅斯管理员

#病毒载体# #基因疗法# #免疫系统# #遗传疾病#

Nature：基因疗法面临免疫系统挑战，我们如何应对？

2024-05-31发表于上海

梅斯管理员

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2024-05-29发表于上海

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2024-03-25发表于上海

梅斯管理员

#基因疗法# #先兆子痫# #能量饮料# #睡眠质量# #遗传性血管水肿#

‘四大顶刊’一周研究导读：发作次数最高减少97%，基因疗法为这种遗传病带来“治愈”可能；能量饮料让年轻人的睡眠质量更差；饮用100%果汁与儿童体重的关系

2024-02-26发表于上海

梅斯管理员

#基因疗法# #遗传性血管水肿# #NTLA-2002#

发作次数最高减少97%！NEJM重磅：基因疗法为这种遗传病带来“治愈”可能！

2024-02-07发表于陕西省

梅斯管理员

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2024-01-28发表于上海

yangchou

全文收起 #基因疗法#先天性肌病包括中央轴空病、线状体肌病、肌小管肌病、先天性纤维类型比例失调症、多轴空病、还原体肌病、球状体肌病等，其共同特点是：①出生时已有病理变化。②肌病非进行性。③形态学角度提示是肌病。约半数有遗传因素。临床甚难鉴别，都有婴儿低肌张力综合征，或稍后出现肌力减退，限于近端或远端，或遍及全身。只有肌活检，有时需有组织化学技术或电镜进行全面分析，才能明确诊断。

2021-08-03