A GLP-Compliant Toxicology and Biodistribution Study of ADVM-062 (AAV.7m8-L-opsin), a Novel Gene Therapy Product Being Developed as a Potential Single Intravitreal Administration for the Treatment of Blue Cone Monochromacy

Hanna, K; Engbers, C; Nieves, J; Sharma, P; Bender, KO; Renz, M; Yu, J; Tai, A; Duncan, S; Szeto, M; Jouttijarvi, H; Cepeda, D; Gelfman, C; Riley, BE; Grishanin, R

MOLECULAR THERAPY, 2022; 30 (4): 589