Dendrimer-N-acetyl-L-cysteine modulates monophagocytic response in adrenoleukodystrophy

Turk, BR; Nemeth, CL; Marx, JS; Tiffany, C; Jones, R; Theisen, B; Kambhampati, S; Ramireddy, R; Singh, S; Rosen, M; Kaufman, ML; Murray, CF; Watkins, PA; Kannan, S; Kannan, R; Fatemi, A

Turk, BR (reprint author), Kennedy Krieger Inst, Moser Ctr Leukodystrophies, Baltimore, MD 21205 USA.; Turk, BR (reprint author), Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21205 USA.

ANNALS OF NEUROLOGY, 2018; 84 (3): 452

Abstract

ObjectiveX-linked adrenoleukodystrophy (ALD) is a neurodegenerative disorder due to mutations in the peroxisomal very long-chain fatty acyl-CoA transp......

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