Midbrain Gene Therapy for AADC Deficiency

Bankiewicz, K; Pearson, T; Kohutnicka, M; Sebastian, WS; Steel, D; Spaull, R; Soo, A; Heales, S; Pons, R; Garcia-Cazorla, A; Ibanez-Mico, S; Sykut-Cegielska, J; Szymanska, K; Opladen, T; Jeltsch, K; Oppeboen, M; Testard, H; Roscher, A; Siegert, S; Willemsen, M; Andrews, S; Ben-Zeev, B; Kurian, M; Zabek, M

MOLECULAR THERAPY, 2023; 31 (4): 4