Proof-of-Concept Studies in Mongolian Gerbils Support Intravitreal Gene Replacement Therapy of Human L-Opsin for Blue Cone Monochromacy

Cepeda, D; Grishanin, R; Nieves, J; Hoeve, JV; Dowd, C; Bender, K; Hanna, K; Levinson, A; Sharma, P; Gasmi, M; Gelfman, C

MOLECULAR THERAPY, 2020; 28 (4): 266