Does Patisiran Reduce Ocular Transthyretin Synthesis? A Pilot Study of Two Cases

Cambieri, C; Marenco, M; Colasanti, T; Mancone, C; Corsi, A; Riminucci, M; Libonati, L; Moret, F; Chimenti, C; Lambiase, A; Conti, F; Garibaldi, M; Inghilleri, M; Ceccanti, M

Ceccanti, M (通讯作者)，Sapienza Univ Rome, Ctr Rare Neuromuscular Dis, Dept Human Neurosci, Rome, Italy.

CURRENT NEUROPHARMACOLOGY, 2023; 21 (12): 2543

Abstract

Background Variant transthyretin-mediated amyloidosis (ATTR-v) is a well-characterized disease affecting the neurologic and cardiovascular systems. Pa......

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