Impact of baseline polyneuropathy severity on patisiran treatment outcomes in the APOLLO trial

Quan, DN; Obici, L; Berk, JL; Ando, Y; Aldinc, E; White, MT; Adams, D

Quan, DN (通讯作者),Univ Colorado Anschutz, 12631 East 17th Ave,Mail Stop B-185, Aurora, CO 80045 USA.

AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2023; 30 (1): 49

Abstract

Objective Assess how baseline polyneuropathy severity impacts response to patisiran regarding neurologic impairment and quality of life (QOL) in patie......

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