Inotersen (transthyretin-specific antisense oligonucleotide) for treatment of transthyretin amyloidosis

Benson, MD; Dasgupta, NR; Monia, BP

Benson, MD (reprint author), Indiana Univ, Dept Pathol & Lab Med, Indianapolis, IN 46204 USA.

NEURODEGENERATIVE DISEASE MANAGEMENT, 2019; 9 (1): 25

Abstract

Hereditary transthyretin amyloidosis (ATTR) is a fatal systemic disease that results from deposition of the misfolded protein transthyretin (TTR) in t......

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