Patisiran in hATTR Amyloidosis: Six-Month Latency Period before Efficacy

Gentile, L; Russo, M; Luigetti, M; Bisogni, G; Di Paolantonio, A; Romano, A; Guglielmino, V; Arimatea, I; Sabatelli, M; Toscano, A; Vita, G; Mazzeo, A

Gentile, L (corresponding author), Univ Messina, Dept Clin & Expt Med, Unit Neurol & Neuromuscular Dis, I-98125 Messina, Italy.

BRAIN SCIENCES, 2021; 11 (4):

Abstract

Hereditary amyloidosis associated with mutations in the transthyretin gene (hATTR) is a progressive devastating disease, with a fatal outcome occurrin......

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