Therapeutic approaches for Duchenne muscular dystrophy

Roberts, TC; Wood, MJA; Davies, KE

Roberts, TC (通讯作者),Univ Oxford, Inst Dev & Regenerat Med, Oxford, England.;Roberts, TC (通讯作者),Univ Oxford, Dept Psychiat, Oxford, England.;Roberts, TC; Davies, KE (通讯作者),MDUK Oxford Neuromuscular Ctr, Oxford, England.;Davies, KE (通讯作者),Univ Oxford, Dept Physiol Anat & Genet, Oxford, England.

NATURE REVIEWS DRUG DISCOVERY, 2023; 22 (11): 917

Abstract

Duchenne muscular dystrophy (DMD) is a monogenic muscle-wasting disorder and a priority candidate for molecular and cellular therapeutics. Although ra......

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